Patient Advocacy

At Ionis Pharmaceuticals, we are dedicated to the discovery and development of novel, first-in-class or best-in-class antisense drugs to address significant unmet medical needs in a wide variety of diseases. Understanding the natural course of disease and the impact that it has on patients is essential to evaluating and developing appropriate medicines. Our Patient Advocacy Group provides support and education for patients and their families, for caregivers and to the community as a whole. We work with the patient community to understand the patient journey, to increase disease awareness, and to give a voice to patients and their families who often feel isolated by their disease.

Clinical Trial Information

We have numerous ongoing clinical trials designed to evaluate our drugs in a variety of health conditions including cardiovascular, metabolic, severe and rare diseases, including neurological disorders, and cancer.
Learn More About Ionis’ Clinical Trials
If you would like more information about a trial or want to enroll in a trial, please visit This government-sponsored Web site lists most ongoing trials including those for which enrollment is currently taking place. Information is searchable by company, by drug candidate, by specific indication and by disease area. For each trial, the investigator is named and enrollment information is provided if appropriate.

Logan Spinal Muscular Atrophy
Lindsey Familial Chylomicronemia Syndrome
Fabio Polyneuropathy Of Hereditary Transthyretin-mediated Amyloidosis